Periodic Reporting for period 1 - BrainCRISPR (In Vivo CRISPR-Based Nanoplatform for Gene Editing: A New Disruptive Avenue for Non-Invasive Treatment of Genetic Brain Diseases)

The revolutionary CRISPR/Cas genome editing technology has enormous potential for treating many genetic diseases. However, delivery of CRISPR machinery to diseased cells within the brain is one of the greatest challenges in medicine today. The ERC Consolidator-funded...